@article{ARH4314,
author = {Christina Elliott and Hussam Al-Humadi and Rodrigo Gutierrez-Quintana and Apostolos Zarros},
title = {Brain N-acetylaspartate accumulation in Canavan disease is not neurotoxic per se: the implications of the first gene replacement therapy study to demonstrate successful post-symptomatic treatment in mice},
journal = {Annals of Research Hospitals},
volume = {2},
number = {4},
year = {2018},
keywords = {},
abstract = {Canavan disease (CD) is identified as a fatal spongiform leukodystrophy caused by missense mutations in the Aspa gene (1,2).},
issn = {2523-0743}, url = {https://arh.amegroups.org/article/view/4314}
}